This rare disease destroys a child’s ability to walk and speak. Could a new drug help?​This rare disease destroys a child’s ability to walk and speak. Could a new drug help? 

This rare disease destroys a child’s ability to walk and speak. Could a new drug help?​This rare disease destroys a child’s ability to walk and speak. Could a new drug help? 

 After a string of denials for rare disease treatments, the FDA greenlit a drug for Hunter syndrome, a progressive illness affecting about 500 Americans.  ​​After a string of denials for rare disease treatments, the FDA greenlit a drug for Hunter syndrome, a progressive illness affecting about 500 Americans. 

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