This rare disease destroys a child’s ability to walk and speak. Could a new drug help?This rare disease destroys a child’s ability to walk and speak. Could a new drug help?
After a string of denials for rare disease treatments, the FDA greenlit a drug for Hunter syndrome, a progressive illness affecting about 500 Americans. After a string of denials for rare disease treatments, the FDA greenlit a drug for Hunter syndrome, a progressive illness affecting about 500 Americans.


